News

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Rare Faces of Medicaid: What’s at Stake for the Rare Community?

Congress is currently considering potentially sweeping funding cuts to Medicaid, a program that provides life-saving...

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Congress: Reauthorize the Rare Pediatric Disease Priority Review Voucher Program

First published July 23, 2024. Updated November 10, 2025 with new content and revisions. The...

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The team presenting their CMT4J pressure-reducing customizable boot at the Harvard Hackathon to an audience that includes CMT patients.
Hack Rare: Engaging the Next Generation of Rare Disease Innovators

By Aditya Tummala, Sydney Wiredu, Derek Liu, and Pranav Ramesh Harvard College, Class of 2026...

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Cover of the report: Preserving Public Trust in the US Newborn Screening System
National Organization for Rare Disorders (NORD) Issues New Report on Lifesaving Newborn Screening Programs

NORD offers comprehensive review on statewide practices related to  screening sample retention, provides policy recommendations February...

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Rare Is Everywhere: Be a Champion to the Rare Disease Community This Feb. 28
Rare Is Everywhere: Be a Champion to the Rare Disease Community This Feb. 28

Think of 10 people you work with, 10 people you went to school with, or...

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NORD, Bionews Partner to Bring Powerful Educational Content to Rare Disease Communities

New Mental Health Video Series Launches February 24 The National Organization for Rare Disorders (NORD®)...

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Highlights from Rare Disease Day 2025
Highlights from Rare Disease Day 2025

From parachuting zebras to "Wicked" stars and breaking news from the NORD® Rare Disease Centers...

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Guest Blog: The Power of Patient Advocacy in Drug Development

The FDA approval of the first treatment for Friedreich’s Ataxia (FA) on Rare Disease Day...

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